BEWARE OF FAKE INSTITUTES WITH SIMILAR NAMES. blank    blank
banner

CRISPR: Treating Sickle Cell & Thalassemia



  Apr 23, 2024

CRISPR: Treating Sickle Cell & Thalassemia



1. What is CRISPR gene-editing?

CRISPR gene-editing is a revolutionary technology that acts like molecular scissors to make precise cuts in DNA. In the context of this therapy, it is used to disable the faulty gene that causes sickle cell disease and beta thalassemia.

2. How does the gene therapy process work?

The process involves extracting bone marrow stem cells from a patient, editing the genes in these cells in a laboratory to correct the mutation, and then re-infusing the modified cells back into the patient. This allows the body to start producing functional hemoglobin.

3. What is the main goal of this gene therapy?

The primary objective of the therapy is to enable the body to produce functional hemoglobin, which is crucial for transporting oxygen. This is particularly important for patients with sickle cell disease and beta thalassemia, who lack functional hemoglobin.

4. How effective has the gene therapy been in clinical trials?

Clinical trials have shown promising results. A significant number of patients with sickle cell disease and beta thalassemia experienced substantial improvements, with many no longer requiring regular blood transfusions.

5. What impact does this gene therapy have?

This gene therapy offers the potential for a permanent cure for patients with these blood disorders, significantly enhancing their quality of life and reducing the lifelong healthcare costs associated with managing these conditions.


SRIRAM's

 


Share:
 

Get a call back

Fill the below form to get free counselling for UPSC Civil Services exam preparation

 
UPSC DAILY CURRENT AFFAIRS

 
RBI’S MONETARY POLICY STANCE
 
French Revolution and India
 
MUSLIM WOMEN UNDER SECTION 125 OF CRPC:
 
BASTILLE DAY
 
INDIA-BASED NEUTRINO OBSERVATORY (INO)
 
India's Critical Minerals Strategy
 
Conflict in Sudan:
 
ASIAN PROTECTIONISM:RESPONSE TO CHINESE OVERCAPACITY
 
IVF Treatments in India
 
Indian quantum cryptography discovery
 
Climate Change : Loss and damage fund
 
INDIA’S FERTILITY RATE DYNAMICS AND IMPACT
 
East China Sea Tensions:Senkaku Islands
 
Green steel and the hydrogen-based DRI production method
 
NABARD's Agri-SURE Fund: Simplifier